Ads
related to: sickle cell disease- Learn About Treatment
Learn About the Treatment Journey.
Watch the Video to Learn More.
- View Discussion Guides
Download Treatment Brochures,
Discussion Guides, and More.
- Patient FAQs
Get Answers to Common Questions.
Understand the Potential Risks.
- Safety and Side Effects
Review the Important Safety
Information & Side Effects.
- Find an ATC
Find an Authorized Treatment Center
On the Official Patient Website.
- Patient Information
View Important Patient Information.
Understand the Treatment.
- Learn About Treatment
Search results
Results From The WOW.Com Content Network
Sickle cell test. A urologist might request this test for men with a higher risk of sickle cell disease. Duplex ultrasound. Sometimes called ultrasonography, this can measure blood flow in your ...
The company's launch of Casgevy, which treats sickle cell disease and transfusion-dependent beta-thalassemia, is in the early innings. ... are the company's islet-cell therapies, which hold the ...
It treats sickle cell disease (SCD) and beta thalassemia, both rare inherited illnesses that affect the function of a person's red blood cells. It has been approved for less than a year in the U.S ...
1 in 10,000 people [2] Spinal muscular atrophy (SMA) is a rare neuromuscular disorder that results in the loss of motor neurons and progressive muscle wasting. [3][4][5] It is usually diagnosed in infancy or early childhood and if left untreated it is the most common genetic cause of infant death. [6] It may also appear later in life and then ...
In 2023, the first drug making use of CRISPR gene editing, Casgevy, was approved for use in the United Kingdom to cure sickle-cell disease and beta thalassemia. [13] [14] Casgevy was approved for use in the United States on December 8, 2023, by the Food and Drug Administration. [15]
Sickle-cell versions of hemoglobin stick to themselves, stacking to form fibers that distort the shape of red blood cells carrying the protein. These sickle-shaped cells no longer flow smoothly through blood vessels, having a tendency to clog or degrade, causing the medical problems associated with this disease. [citation needed]
Ad
related to: sickle cell disease