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CRISPR Therapeutics' first therapy is called Casgevy. It treats sickle cell disease (SCD) and beta thalassemia, both rare inherited illnesses that affect the function of a person's red blood cells.
They include other target indications for povetacicept and suzetrigine, a next-generation nonopioid pain drug (VX-993), a messenger RNA therapy for CF (VX-552), and a therapy targeting myotonic ...
In December 2023, the FDA approved the first gene therapy in the US to treat patients with Sickle Cell Disease (SCD). The FDA approved two milestone treatments, Casgevy and Lyfgenia, representing the first cell-based gene therapies for the treatment of SCD. [57]
Vivek Ganapathy Ramaswamy (/ v ɪ ˈ v eɪ k r ɑː m ə ˈ s w ɑː m iː /; [1] [2] vih-VAYK rah-mə-SWAH-mee; born August 9, 1985) is an American entrepreneur.He founded Roivant Sciences, a pharmaceutical company, in 2014.
Options include interleukin-2, which is a standard therapy for advanced renal cell carcinoma. [99] From 2007 to 2013, seven new treatments have been approved specifically for mRCC (sunitinib, temsirolimus, bevacizumab, sorafenib, everolimus, pazopanib and axitinib). [ 8 ]
Sean 'Diddy' Combs to appear in court for bail hearing: Live updates. Sean "Diddy" Combs is set to appear in court for a bail hearing to determine if he remains in jail until trial. The music ...
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