Ads
related to: new cure for sickle cell disease- What Is LYFGENIA?
Learn About LYFGENIA As
A Treatment Option.
- Steps To Treatment
See A Breakdown Of
Treatment With LYFGENIA.
- How Does LYFGENIA Work?
See How It Works & The
Treatment Process.
- my bluebird support
Learn More About This Resource
For Patients On LYFGENIA.
- FAQs
Your LYFGENIA Questions. Answered.
Review Patient Information.
- Studies & Results
Review How LYFGENIA Was
Studied & The Results.
- What Is LYFGENIA?
Search results
Results From The WOW.Com Content Network
(Reuters) -U.S. drugmaker Pfizer said on Wednesday it is withdrawing its sickle cell disease therapy Oxbryta in all markets where it is approved and discontinuing all studies and access programs ...
CEO Andrew Obenshain said the latest restructuring would help support the marketing of its three gene therapies, including the recently approved sickle cell disease treatment, Lyfgenia.
This treatment thus avoids the need for regular, costly blood transfusions. [13] [14] In December 2023, the FDA approved the first gene therapy in the US to treat patients with Sickle Cell Disease (SCD). The FDA approved two milestone treatments, Casgevy and Lyfgenia, representing the first cell-based gene therapies for the treatment of SCD. [57]
Inaxaplin is already in a phase 3 trial for treating APOL1-mediated kidney disease. This indication would open up an even bigger market than CF to Vertex if the experimental drug wins approval.
However, in systemic lupus erythematosus it is 4 to 14%, [106] and in sickle cell disease, it ranges from 20 to 40%. [107] Up to 4% of people who develop a pulmonary embolism go on to develop chronic thromboembolic disease including pulmonary hypertension. [ 40 ]
Vivek Ganapathy Ramaswamy (/ v ɪ ˈ v eɪ k r ɑː m ə ˈ s w ɑː m iː /; [1] [2] vih-VAYK rah-mə-SWAH-mee; born August 9, 1985) is an American entrepreneur.He founded Roivant Sciences, a pharmaceutical company, in 2014.
Socioeconomic factors are the related cause, alongside it presenting barriers to treatment in the disease. [30] Sickle cell disease is more susceptible to be found in those of descent from places such as those in the Mediterranean, Italy, Turkey, and Greece, as well as Africa and regions of South and Central America. [48]
Sickle-cell anemia, which can cause blood cells to clump up and block blood vessels, can also lead to stroke. Stroke is the second leading cause of death in people under 20 with sickle-cell anemia. [52] Air pollution may also increase stroke risk. [53]
Ad
related to: new cure for sickle cell disease